| Emerging issues in AAV-mediated in vivo gene therapy P Colella, G Ronzitti, F Mingozzi Molecular Therapy-Methods & Clinical Development 8, 87-104, 2018 | 487 | 2018 |
| The regulation of synaptic function by α-synuclein S Bellani, VL Sousa, G Ronzitti, F Valtorta, J Meldolesi, E Chieregatti Communicative & integrative biology 3 (2), 106-109, 2010 | 142 | 2010 |
| Antigen-selective modulation of AAV immunogenicity with tolerogenic rapamycin nanoparticles enables successful vector re-administration A Meliani, F Boisgerault, R Hardet, S Marmier, F Collaud, G Ronzitti, ... Nature communications 9 (1), 1-13, 2018 | 126 | 2018 |
| Influence of pre-existing anti-capsid neutralizing and binding antibodies on AAV vector transduction Z Fitzpatrick, C Leborgne, E Barbon, E Masat, G Ronzitti, ... Molecular Therapy-Methods & Clinical Development 9, 119-129, 2018 | 100 | 2018 |
| Selective disruption of the E-cadherin–catenin system by an algal toxin G Ronzitti, F Callegari, C Malaguti, GP Rossini British journal of cancer 90 (5), 1100-1107, 2004 | 89 | 2004 |
| IgG-cleaving endopeptidase enables in vivo gene therapy in the presence of anti-AAV neutralizing antibodies C Leborgne, E Barbon, JM Alexander, H Hanby, S Delignat, DM Cohen, ... Nature Medicine 26 (7), 1096-1101, 2020 | 88 | 2020 |
| TAAR1 modulates cortical glutamate NMDA receptor function S Espinoza, G Lignani, L Caffino, S Maggi, I Sukhanov, D Leo, L Mus, ... Neuropsychopharmacology 40 (9), 2217-2227, 2015 | 88 | 2015 |
| Human immune responses to adeno-associated virus (AAV) vectors G Ronzitti, DA Gross, F Mingozzi Frontiers in Immunology 11, 670, 2020 | 87 | 2020 |
| Azaspiracid-1 alters the E-cadherin pool in epithelial cells G Ronzitti, P Hess, N Rehmann, GP Rossini Toxicological sciences 95 (2), 427-435, 2007 | 78 | 2007 |
| A cytolytic assay for the measurement of palytoxin based on a cultured monolayer cell line M Bellocci, G Ronzitti, A Milandri, N Melchiorre, C Grillo, R Poletti, ... Analytical Biochemistry 374 (1), 48-55, 2008 | 77 | 2008 |
| Rescue of Pompe disease in mice by AAV-mediated liver delivery of secretable acid α-glucosidase F Puzzo, P Colella, MG Biferi, D Bali, NK Paulk, P Vidal, F Collaud, ... Science translational medicine 9 (418), eaam6375, 2017 | 76 | 2017 |
| Enhanced liver gene transfer and evasion of preexisting humoral immunity with exosome-enveloped AAV vectors A Meliani, F Boisgerault, Z Fitzpatrick, S Marmier, C Leborgne, F Collaud, ... Blood advances 1 (23), 2019-2031, 2017 | 64 | 2017 |
| GRP78 clustering at the cell surface of neurons transduces the action of exogenous alpha-synuclein S Bellani, A Mescola, G Ronzitti, H Tsushima, S Tilve, C Canale, ... Cell Death & Differentiation 21 (12), 1971-1983, 2014 | 59 | 2014 |
| Exposure to wild-type AAV drives distinct capsid immunity profiles in humans K Kuranda, P Jean-Alphonse, C Leborgne, R Hardet, F Collaud, ... The Journal of clinical investigation 128 (12), 5267-5279, 2018 | 57 | 2018 |
| Low-dose liver-targeted gene therapy for Pompe disease enhances therapeutic efficacy of ERT via immune tolerance induction S Han, G Ronzitti, B Arnson, C Leborgne, S Li, F Mingozzi, D Koeberl Molecular Therapy-Methods & Clinical Development 4, 126-136, 2017 | 53 | 2017 |
| Exogenous α-synuclein decreases raft partitioning of Cav2. 2 channels inducing dopamine release G Ronzitti, G Bucci, M Emanuele, D Leo, TD Sotnikova, LV Mus, ... Journal of Neuroscience 34 (32), 10603-10615, 2014 | 51 | 2014 |
| A translationally optimized AAV-UGT1A1 vector drives safe and long-lasting correction of Crigler-Najjar syndrome G Ronzitti, G Bortolussi, R Van Dijk, F Collaud, S Charles, C Leborgne, ... Molecular Therapy-Methods & Clinical Development 3, 16049, 2016 | 44 | 2016 |
| Parkin regulates kainate receptors by interacting with the GluK2 subunit AM Maraschi, A Ciammola, A Folci, F Sassone, G Ronzitti, G Cappelletti, ... Nature communications 5 (1), 1-10, 2014 | 41 | 2014 |
| Autophagy determines efficiency of liver‐directed gene therapy with adeno‐associated viral vectors M Hösel, A Huber, S Bohlen, J Lucifora, G Ronzitti, F Puzzo, F Boisgerault, ... Hepatology 66 (1), 252-265, 2017 | 30 | 2017 |
| Yessotoxin induces the accumulation of altered E-cadherin dimers that are not part of adhesive structures in intact cells G Ronzitti, GP Rossini Toxicology 244 (2-3), 145-156, 2008 | 28 | 2008 |
piter bosmaassociate professor of Gene Therapy, Tytgat Institute, AMC,AmsterdamEmail confirmado em amc.uva.nl
